Efficacy and safety of Velmanase alfa in the treatment of patients with alpha-mannosidosis: results from the core and extension phase analysis of a phase III multicentre, double-blind, randomised, placebo-controlled trial
- Borgwardt, L.
- Guffon, N.
- Amraoui, Y.
- Dali, C.I.
- De Meirleir, L.
- Gil-Campos, M.
- Heron, B.
- Geraci, S.
- Ardigò, D.
- Cattaneo, F.
- Fogh, J.
- Van den Hout, J.M.H.
- Beck, M.
- Jones, S.A.
- Tylki-Szymanska, A.
- Haugsted, U.
- Lund, A.M.
ISSN: 1573-2665, 0141-8955
Ano de publicación: 2018
Volume: 41
Número: 6
Páxinas: 1215-1223
Tipo: Artigo