Health Related Quality of Life, Disability, and Pain in Alpha Mannosidosis: Long-Term Data of Enzyme Replacement Therapy With Velmanase Alfa (Human Recombinant Alpha Mannosidase)
- Borgwardt, L.
- Guffon, N.
- Amraoui, Y.
- Jones, S.A.
- De Meirleir, L.
- Lund, A.M.
- Gil-Campos, M.
- Van den Hout, J.M.P.
- Tylki-Szymanska, A.
- Geraci, S.
- Ardigò, D.
- Cattaneo, F.
- Harmatz, P.
- Phillips, D.
Revista:
Journal of Inborn Errors of Metabolism and Screening
ISSN: 2326-4594, 2326-4098
Año de publicación: 2018
Volumen: 6
Tipo: Artículo