Health Related Quality of Life, Disability, and Pain in Alpha Mannosidosis: Long-Term Data of Enzyme Replacement Therapy With Velmanase Alfa (Human Recombinant Alpha Mannosidase)

  1. Borgwardt, L.
  2. Guffon, N.
  3. Amraoui, Y.
  4. Jones, S.A.
  5. De Meirleir, L.
  6. Lund, A.M.
  7. Gil-Campos, M.
  8. Van den Hout, J.M.P.
  9. Tylki-Szymanska, A.
  10. Geraci, S.
  11. Ardigò, D.
  12. Cattaneo, F.
  13. Harmatz, P.
  14. Phillips, D.
Revista:
Journal of Inborn Errors of Metabolism and Screening

ISSN: 2326-4594 2326-4098

Año de publicación: 2018

Volumen: 6

Tipo: Artículo

DOI: 10.1177/2326409818796854 GOOGLE SCHOLAR lock_openAcceso abierto editor