Isogenic GAA-KO Murine Muscle Cell Lines Mimicking Severe Pompe Mutations as Preclinical Models for the Screening of Potential Gene Therapy Strategies

  1. Aguilar-González, A.
  2. González-Correa, J.E.
  3. Barriocanal-Casado, E.
  4. Ramos-Hernández, I.
  5. Lerma-Juárez, M.A.
  6. Greco, S.
  7. Rodríguez-Sevilla, J.J.
  8. Molina-Estévez, F.J.
  9. Montalvo-Romeral, V.
  10. Ronzitti, G.
  11. Sánchez-Martín, R.M.
  12. Martín, F.
  13. Muñoz, P.
Journal:
International Journal of Molecular Sciences

ISSN: 1422-0067 1661-6596

Year of publication: 2022

Volume: 23

Issue: 11

Type: Article

DOI: 10.3390/IJMS23116298 GOOGLE SCHOLAR lock_openOpen access editor