Lentiviral gene therapy reverts GPIX expression and phenotype in Bernard-Soulier syndrome type C

  1. Martinez-Navajas, G.
  2. Ceron-Hernandez, J.
  3. Simon, I.
  4. Lupiañez, P.
  5. Diaz-McLynn, S.
  6. Perales, S.
  7. Modlich, U.
  8. Guerrero, J.A.
  9. Martin, F.
  10. Sevivas, T.
  11. Lozano, M.L.
  12. Rivera, J.
  13. Ramos-Mejia, V.
  14. Tersteeg, C.
  15. Real, P.J.
Journal:
Molecular Therapy - Nucleic Acids

ISSN: 2162-2531

Year of publication: 2023

Volume: 33

Pages: 75-92

Type: Article

DOI: 10.1016/J.OMTN.2023.06.008 GOOGLE SCHOLAR lock_openOpen access editor

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