Publications by the researcher in collaboration with Iris Ramos Hernández (3)

2022

  1. Isogenic GAA-KO Murine Muscle Cell Lines Mimicking Severe Pompe Mutations as Preclinical Models for the Screening of Potential Gene Therapy Strategies

    International Journal of Molecular Sciences, Vol. 23, Núm. 11

2020

  1. Development of Cellular Models to Study Efficiency and Safety of Gene Edition by Homologous Directed Recombination Using the CRISPR/Cas9 System

    Cells, Vol. 9, Núm. 6

  2. Genome-edited adult stem cells: Next-generation advanced therapy medicinal products

    Stem Cells Translational Medicine, Vol. 9, Núm. 6, pp. 674-685