Lentiviral gene therapy reverts GPIX expression and phenotype in Bernard-Soulier syndrome type C
- Martinez-Navajas, G.
- Ceron-Hernandez, J.
- Simon, I.
- Lupiañez, P.
- Diaz-McLynn, S.
- Perales, S.
- Modlich, U.
- Guerrero, J.A.
- Martin, F.
- Sevivas, T.
- Lozano, M.L.
- Rivera, J.
- Ramos-Mejia, V.
- Tersteeg, C.
- Real, P.J.
Journal:
Molecular Therapy - Nucleic Acids
ISSN: 2162-2531
Year of publication: 2023
Volume: 33
Pages: 75-92
Type: Article