MARIA MERCEDES
GIL CAMPOS
Sophia Children's Hospital
Róterdam, HolandaPublicaciones en colaboración con investigadores/as de Sophia Children's Hospital (3)
2018
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Comprehensive long-term efficacy and safety of recombinant human alpha-mannosidase (velmanase alfa) treatment in patients with alpha-mannosidosis
Journal of Inherited Metabolic Disease, Vol. 41, Núm. 6, pp. 1225-1233
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Efficacy and safety of Velmanase alfa in the treatment of patients with alpha-mannosidosis: results from the core and extension phase analysis of a phase III multicentre, double-blind, randomised, placebo-controlled trial
Journal of Inherited Metabolic Disease, Vol. 41, Núm. 6, pp. 1215-1223
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Health Related Quality of Life, Disability, and Pain in Alpha Mannosidosis: Long-Term Data of Enzyme Replacement Therapy With Velmanase Alfa (Human Recombinant Alpha Mannosidase)
Journal of Inborn Errors of Metabolism and Screening, Vol. 6